prevention of diabetes due to total pancreatectomy
All entries for: Rare Disease
June 11, 2026
Shanghai Simnova Biotechnology Co. Ltd.
Investment: Designated
treatment of small cell lung cancer
Disease Area: Rare Diseases
June 11, 2026
Alkermes Inc.
Investment: Designated
treatment of idiopathic hypersomnia
Disease Area: Rare Diseases
June 11, 2026
GRT Therapeutics Inc.
Investment: Designated
treatment of Duchenne muscular dystrophy
Disease Area: Rare Diseases
June 10, 2026
Beren Therapeutics
Investment: Later Stage VC
Beren Therapeutics raised $300 million to support the potential commercial launch of adrabetadex, an FDA Breakthrough Therapy-designated cyclodextrin therapy under Priority Review for the treatment of infantile-onset Niemann-Pick disease type C, a rare and rapidly fatal pediatric neurodegenerative disorder.
Disease Area: Rare Diseases
June 9, 2026
Ratio Therapeutics Inc.
Investment: Designated
treatment of soft tissue sarcoma
Disease Area: Rare Diseases
June 8, 2026
Langxin Qisheng (Suzhou) Biopharmaceutical Co. Ltd.
Investment: Designated
treatment of PROM1-associated retinal dystrophy
Disease Area: Rare Diseases
June 8, 2026
Kalevala Therapeutics Inc.
Investment: Designated
treatment of alternating hemiplegia
Disease Area: Rare Diseases
June 8, 2026
Infinant Health
Investment: Later Stage VC
Infinant Health raised $39.25 million to advance INF108, an FDA-designated orphan drug and rare pediatric disease-designated live biotherapeutic for the prevention of necrotizing enterocolitis, a rare and life-threatening intestinal condition primarily affecting preterm infants.
Disease Area: Rare Diseases
June 8, 2026
City Therapeutics
Investment: Early Stage VC
City Therapeutics raised $99.5 million to advance CITY-FXI, a next-generation RNAi therapy in Phase 1 clinical development for the prevention of thromboembolic diseases including stroke and deep vein thrombosis, as well as CITY-RBP4, an RNAi candidate for Stargardt disease, a rare inherited form of juvenile macular degeneration.
Disease Area: Rare Diseases