FDA orphan drug designation: treatment of idiopathic pulmonary fibrosis
All entries for: Rare Disease
October 24, 2025
Zenith Epigenetics Ltd.
Orphan Drug Designation
FDA orphan drug designation: treatment of nuclear protein in testis (NUT) carcinoma
Disease Area: Rare Diseases
October 23, 2025
Shanghai CirCode Biomed Co. Ltd.
Orphan Drug Designation
FDA orphan drug designation: treatment of thromboangiitis obliterans
Disease Area: Rare Diseases
October 23, 2025
Jazz Pharmaceuticals Ireland Limited
Orphan Drug Designation
FDA orphan drug designation: treatment of esophageal cancer
Disease Area: Rare Diseases
October 22, 2025
ArKri Therapeutics
Orphan Drug Designation
FDA orphan drug designation: treatment of Huntington’s disease
Disease Area: Rare Diseases
October 22, 2025
Curlim S.A.S
Orphan Drug Designation
FDA orphan drug designation: treatment of Charcot-Marie-Tooth disease (CMT)
Disease Area: Rare Diseases
October 22, 2025
Dewpoint Therapeutics Inc.
Orphan Drug Designation
FDA orphan drug designation: treatment of gastric cancer, including gastroesophageal junction cancer
Disease Area: Rare Diseases
October 22, 2025
Pangenix Pharma Limited
Orphan Drug Designation
FDA orphan drug designation: treatment of chronic pancreatitis
Disease Area: Rare Diseases
October 21, 2025
Schrödinger Inc.
Orphan Drug Designation
FDA orphan drug designation: treatment of Waldenstrom’s macroglobulinemia
Disease Area: Rare Diseases
October 21, 2025
Revolution Medicines Inc.
Orphan Drug Designation
FDA orphan drug designation: treatment of pancreatic cancer
Disease Area: Rare Diseases
