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Rare Disease Tracker
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Rare Disease Tracker
Most Favored Nation Tracker
Methodology
All entries for: Shanghai Vitalgen BioPharma Co., Ltd.
January 23, 2026
Shanghai Vitalgen BioPharma Co., Ltd.
Orphan Drug Designation
treatment of aromatic L-amino acid decarboxylase (AADC) deficiency
Disease Area:
Rare Disease
Source
Source
January 13, 2026
Shanghai Vitalgen BioPharma Co., Ltd.
Orphan Drug Designation
treatment of Gaucher disease
Disease Area:
Rare Disease
Source
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