FDA orphan drug designation: treatment of malignant glioma
All entries for: Rare Disease
October 16, 2025
Resolute Science Inc.
Orphan Drug Designation
FDA orphan drug designation: treatment of soft tissue sarcomas
Disease Area: Rare Diseases
October 16, 2025
ODDIFACT SAS
Orphan Drug Designation
FDA orphan drug designation: treatment of bullous pemphigoid
Disease Area: Rare Diseases
October 16, 2025
Amgen Inc.
Orphan Drug Designation
FDA orphan drug designation: treatment of systemic sclerosis
Disease Area: Rare Diseases
October 16, 2025
Sanegene Bio USA Inc.
Orphan Drug Designation
FDA orphan drug designation: treatment of complement 3 glomerulopathy
Disease Area: Rare Diseases
October 16, 2025
Immusoft CA Inc.
Orphan Drug Designation
FDA orphan drug designation: treatment of mucopolysaccharidosis type II
Disease Area: Rare Diseases
October 16, 2025
Biogenera SpA
Orphan Drug Designation
FDA orphan drug designation: treatment of soft tissue sarcoma
Disease Area: Rare Diseases
October 16, 2025
Shanghai Henlius Biotech Inc.
Orphan Drug Designation
FDA orphan drug designation: treatment of thymic epithelial tumors
Disease Area: Rare Diseases
October 16, 2025
AskBio Inc.
Orphan Drug Designation
FDA orphan drug designation: treatment of Pompe disease
Disease Area: Rare Diseases
October 16, 2025
Remedy Plan Inc
Orphan Drug Designation
FDA orphan drug designation: treatment of acute myeloid leukemia
Disease Area: Rare Diseases
